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Brogidirsen
Brogidirsen
Product Name
Brogidirsen
CAS
2409088-11-3
MF
MW
0
EINECS
MOL File
Mol File
Chemical Properties
Sequence
RNA, [P-deoxy-P-(dimethylamino)](2′,3′-dideoxy-2′,3′-imino-2′,3′-seco)(2′a→5′)(m5U-m5U-G-m5U-G-m5U-C-m5U-m5U-m5U-C-m5U-m5U-C-m5U-G-m5U-m5U-A-G-C-C-A-C)
Usage And Synthesis
Uses
Brogidirsen exerts the stimulatory function of synthesis of functional dystrophin[1].
References
[1] International Nonproprietary Names for Pharmaceutical Substances (INN). WHO Drug Information. 2022. 36(2):337.
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